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Journal articles
AAV-mediated transfer of FKRP shows therapeutic efficacy in a murine model but requires control of gene expression
Evelyne Gicquel
1
Natacha Maizonnier
1
Steven Foltz
2
William Martin
Nathalie Bourg
1
Fedor Svinartchouk
1
Karine Charton
1
Aaron Beedle
2
Isabelle Richard
1
Evelyne Gicquel 1
Author IdHAL : evelyne-gicquel
Natacha Maizonnier 1
Author
Steven Foltz 2
Author
William Martin
Author
Nathalie Bourg 1
Author IdHAL : nathalie-bourg
Fedor Svinartchouk 1
Author
Karine Charton 1
Author
Aaron M. Beedle 2
Author
Isabelle Richard 1
Author
1
INTEGRARE - Approches génétiques intégrées et nouvelles thérapies pour les maladies rares (1 bis rue de l'Internationale, 91002 Évry Cedex - France)
- UEVE - Université d'Évry-Val-d'Essonne (Boulevard François Mitterrand 91025 Evry Cedex - France)
- INSERM - Institut National de la Santé et de la Recherche Médicale : UMR_S951 (101, rue de Tolbiac, 75013 Paris - France)
- GENETHON 3 (France)
- EPHE - École pratique des hautes études (4-14 Rue Ferrus, 75014 Paris - France)
- PSL - Université Paris sciences et lettres (60 rue Mazarine 75006 Paris - France)
2
University of Georgia [USA] (Athens, GA 30602 - United States)
Document type :
Journal articles
Complete list of metadatas
https://hal-univ-evry.archives-ouvertes.fr/hal-02177575
Contributor : Evelyne Gicquel <>
Submitted on : Tuesday, July 9, 2019 - 10:57:12 AM
Last modification on : Friday, September 18, 2020 - 2:34:59 PM
Contributor : Evelyne Gicquel <>
Submitted on : Tuesday, July 9, 2019 - 10:57:12 AM
Last modification on : Friday, September 18, 2020 - 2:34:59 PM
Links full text
Identifiers
- HAL Id : hal-02177575, version 1
- DOI : 10.1093/hmg/ddx066
Collections
UNIV-EVRY | INTEGRARE | UNIV-PARIS-SACLAY | EPHE | PSL
Citation
Evelyne Gicquel, Natacha Maizonnier, Steven Foltz, William Martin, Nathalie Bourg, et al.. AAV-mediated transfer of FKRP shows therapeutic efficacy in a murine model but requires control of gene expression. Human Molecular Genetics, Oxford University Press (OUP), 2017, 26 (10), pp.1952-1965. ⟨10.1093/hmg/ddx066⟩. ⟨hal-02177575⟩
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