Skip to Main content Skip to Navigation
Journal articles

AAV-mediated transfer of FKRP shows therapeutic efficacy in a murine model but requires control of gene expression

Evelyne Gicquel 1 Natacha Maizonnier 1 Steven Foltz 2 William Martin Nathalie Bourg 1 Fedor Svinartchouk 1 Karine Charton 1 Aaron M. Beedle 2 Isabelle Richard 1 
1 INTEGRARE - Approches génétiques intégrées et nouvelles thérapies pour les maladies rares
2 University of Georgia [USA]
Keywords : Muscle Dystrophy LGMD FKRP
Document type :
Journal articles
Complete list of metadata
https://hal-univ-evry.archives-ouvertes.fr/hal-02177575
Contributor : Evelyne Gicquel Connect in order to contact the contributor
Submitted on : Tuesday, July 9, 2019 - 10:57:12 AM
Last modification on : Wednesday, November 17, 2021 - 12:33:16 PM

Links full text

pubmedcentral

Identifiers

Collections

EPHE | UNIV-EVRY | PSL | INTEGRARE | UNIV-PARIS-SACLAY | GS-HEALTH-DRUG-SCIENCES

Citation

Evelyne Gicquel, Natacha Maizonnier, Steven Foltz, William Martin, Nathalie Bourg, et al.. AAV-mediated transfer of FKRP shows therapeutic efficacy in a murine model but requires control of gene expression. Human Molecular Genetics, Oxford University Press (OUP), 2017, 26 (10), pp.1952-1965. ⟨10.1093/hmg/ddx066⟩. ⟨hal-02177575⟩

Export

BibTeX TEI DC DCterms EndNote Datacite

Share

Metrics

Record views

26

Université d'Évry-Val-d'Essonne

Boulevard François Mitterrand
91025 Evry Cedex
www.univ-evry.fr

Les gènes de la connaissance